Research Highlights

January 2013
Molecular Therapy;Jan2013, Vol. 21 Issue 1, p4
Academic Journal
The article offers information on several studies related to gene and cell therapy. It mentions a study which showed the use of induced pluripotent stem (iPS) cells in examining the response of diseased cells to drugs. It says that a drug which can increase antisense oligonucleotide therapy's effectiveness for treating Duchenne muscular dystrophy (DMD) was revealed in another study. It adds that a study found the existence of somatic copy-number variations (CNVs) in skin fibroblasts' genomes.


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